He notes that AAV is already being used in gene therapy clinical trials for Parkinson's disease, hemophilia, and vision disorders. (cen.acs.org)
Vectors designed and manufactured at St. Jude have already helped transform the lives of patients participating in gene therapy clinical trials for immune and blood disorders. (stjude.org)
Several gene therapy clinical trials using gene - modified hematopoietic stem cells have shown therapeutic efficacy in multiple disease areas. (research.hsr.it)