Through regional networks in the U.S. like the Pediatric Neuromuscular Clinical Research (PNCR) Network and Project Cure, and international organizations such as the International Coordinating Committee (ICC) and TREAT - NMD, the SMA community has collaborated effectively on recruiting patients, establishing standards of care, standardizing outcome measures, and supporting multi-site clinical efforts, such as the Biomarkers for SMA (BforSMA) and the PNCR
Network Natural History studies.
Not exact matches
The
study was sponsored by the Geological Society of America, the American Museum of
Natural History and the Smithsonian Institution's Marine Science
Network.
The Pediatric Neuromuscular Clinical Research
Network will launch with a
natural history study of patients suffering from spinal muscular atrophy.
SMA
Natural History Study The PNCR
Network helped to characterize the SMA patient population and increase understanding of the stages of disease progression through the ongoing greater than 24 month SMA
Natural History Study (NHS).
Analysis of this data revealed a set of candidate biomarkers which were then tested against over 150 longitudinal samples from an SMA
natural history study by the Pediatric Neuromuscular Clinical Research
Network.