Novel therapies such as gene therapy represent an opportunity to fix the faulty gene responsible and allow these children the chance to have a normal life.
Not exact matches
SiteOne is dedicated to developing
novel pain therapeutics to safely, effectively and efficiently treat acute and chronic pain without the limitations of existing pain
therapies,
such as NSAIDs or opioids.
Novels are particularly rich in their explorations of these issues, though such understanding need not be gained only from novels: In The Therapy of Desire (1994) Nussbaum seeks» not always successfully» to discover in certain Hellenistic thinkers a distinctively philosophical account of the value of the emo
Novels are particularly rich in their explorations of these issues, though
such understanding need not be gained only from
novels: In The Therapy of Desire (1994) Nussbaum seeks» not always successfully» to discover in certain Hellenistic thinkers a distinctively philosophical account of the value of the emo
novels: In The
Therapy of Desire (1994) Nussbaum seeks» not always successfully» to discover in certain Hellenistic thinkers a distinctively philosophical account of the value of the emotions.
She is interested in
novel therapies to prevent and manage HSV infection,
such as antiviral agents and vaccines.
Trapnell and Suzuki were prompted to test the
novel macrophage transplantation
therapy by studies showing that resident macrophage populations (
such as those residing in the lung) can self - maintain without the cells having to regenerate directly from the bone marrow.
«The addition of osteocalcin as a metabolic regulator may one day lead to
novel therapies, but we need to understand much better how it works and how it fits into physiology before
such therapies can be attempted in humans,» says endocrinologist Mitch Lazar, director of the Institute for Diabetes, Obesity, and Metabolism at the University of Pennsylvania.
A number of these trials represent completely
novel classes of
therapy,
such as employing fragments of RNA that interfere with problem genes or developing vaccines meant to quell drug addiction.
This
novel approach may have ramifications for other inflammatory diseases including rheumatoid arthritis and psoriasis, as well as for other biologic
therapies (
such as Humira) used to treat these conditions.
So far, DARPA has released two calls for grant applications, with at least one more likely: The first, called SUBNETS (Systems - Based Neurotechnology for Emerging
Therapies), asks researchers to develop
novel, wireless devices,
such as deep brain stimulators, that can cure neurological disorders
such as posttraumatic stress (PTS), major depression, and chronic pain.
Shoemaker has been studying gene
therapy as a
novel way to treat diseases
such as botulism, a rare but serious paralytic illness caused by a nerve toxin that is produced by the bacterium Clostridium botulinum.
Therefore, we are investigating mechanisms of network hypersynchronization in AD and testing
novel therapies to prevent
such deficits.
Finally, Pollard wants to close the loop by incorporating code - writing approaches,
such as genome editing using CRISPR - based approaches and synthetic biology, which are needed to test and validate hypotheses and could also provide
novel therapies.
As demonstrated by the breadth of clinical trial involvement shown above, CCIR members are testing the utility of immune checkpoint blockade in lymphoma (shown by Dr. Allison to be effective against melanoma), genetic engineering in cell
therapy (e.g., CD19, CXCR2, TGF - β DNR), and TLR agonists or IL - 2 in vaccine formulations as well as some
novel combination
therapies,
such as the infusion of tumor - reactive lymphocytes from HLA - matched donors who were vaccinated with a lymphoma idiotype.
I - Stem, the Institute for Stem cell
Therapy and Exploration of Monogenic Diseases, has signed an agreement with Swissbased healthcare company Roche to use I - Stem's technologies in discovering
novel therapies to treat devastating central nervous system (CNS) diseases
such as Alzheimer's, schizophrenia, depression and anxiety.
In the last decade, Foxp3 + Treg cells have raised the hope for
novel cell - based
therapies to achieve tolerance in clinical settings of unwanted immune responses
such as autoimmunity and graft rejection.
This «humanized» mouse is susceptible to human liver infections and responds to human drug treatments, providing a new way to test
novel therapies for debilitating human liver diseases and other diseases with liver involvement
such as malaria.
Having
such biomarkers will greatly enhance the development of new and
novel therapies for this disabling disorder.»
A major goal is to integrate genetic, clinical, and laboratory features to identify patients who share disease biology and clinical outcome,
such that
therapies, both existing and
novel, can be better targeted.
The approach is to use clinically relevant tumor models
such as patient - derived xenografts (PDXs), as well as humanized and immunocompetent transgenic tumor - bearing mice to design rational combinations of
novel and emerging cancer
therapies, including tumor - targeting and immune - stimulating
therapies, to ultimately improve treatment outcomes for cancer patients.
Nutritional
therapy has emerged as a
novel approach to control appetite and the role of nutrigenomics as an early nutritional
therapy may assist genes to delay liver and brain diseases
such as Parkinson's disease (PD) and Huntington's disease (HD) that are associated with aging.
Using my degree in Recreational
Therapy I have worked with autistic children, In this
novel I wanted a story that would lift their value in the world while at the same time highlight the difficulty raising
such a special child.