11/10/2008 UC San Diego Medical Center
Offers Gene Therapy Clinical Trial for Advanced Heart Failure UC San Diego Medical Center is currently enrolling patients in a Phase 2 clinical trial of an investigational drug for the treatment of advanced heart failure.
Boston Children's Hospital has
offered non-exclusive licenses to for - profit entities on a patent developed by Orkin's laboratory regarding BCL11A, a genetic switch regulating hemoglobin production that is expected to form the basis of
clinical trials for
gene therapy and
gene editing for sickle cell disease and thalassemia.