Sentences with phrase «sma natural history study»

Analysis of this data revealed a set of candidate biomarkers which were then tested against over 150 longitudinal samples from an SMA natural history study by the Pediatric Neuromuscular Clinical Research Network.

SMA Natural History Study The PNCR Network helped to characterize the SMA patient population and increase understanding of the stages of disease progression through the ongoing greater than 24 month SMA Natural History Study (NHS).

Not exact matches

Through regional networks in the U.S. like the Pediatric Neuromuscular Clinical Research (PNCR) Network and Project Cure, and international organizations such as the International Coordinating Committee (ICC) and TREAT - NMD, the SMA community has collaborated effectively on recruiting patients, establishing standards of care, standardizing outcome measures, and supporting multi-site clinical efforts, such as the Biomarkers for SMA (BforSMA) and the PNCR Network Natural History studies.

SMA Foundation Patient Advisory Board member Amelie Gubitz finished the discussion by suggesting these issues be followed in natural history studies.