Sentences with phrase «based gene therapy company»

• LogicBio Therapeutics, a Foster City, Calif. - based gene therapy company, raised $ 45 million in Series B funding.

Not exact matches

• Myonexus Therapeutics, a New Albany, Oh. - based clinical - stage biotechnology company developing transformative gene therapies for limb - girdle muscular dystrophies, raised $ 2.5 million in seed funding.

• Vineti, a San Francisco - based cell and gene therapy software and analytics company, raised $ 13.75 million in Series A funding.

US - based pharmaceutical company Gilead Sciences entered the chimeric antigen receptor (CAR) T - cell therapy business through its acquisition of Kite Pharma, and Australian biopharma company CSL Behring acquired US - based Calimmune, a company that develops clinical - stage gene therapy solutions.

He and his lab, for example, along with the company Neurologix based in Fort Lee, N.J., are conducting a clinical trial to test a similar gene - therapy treatment for Parkinson's disease.

AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, announced in July 2016 that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy Designation for the treatment based on preliminary clinical results from the trial of AVXStherapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, announced in July 2016 that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy Designation for the treatment based on preliminary clinical results from the trial of AVXSTherapy Designation for the treatment based on preliminary clinical results from the trial of AVXS - 101.

PNP Therapeutics, Inc. — a company based on a gene - therapy technology developed by scientists at Southern Research Institute and the University of Alabama at Birmingham (UAB)-- has found an approach that has abolished otherwise unmanageable human cancers in preclinical rodent studies.

Chris Mason is a Co-Founder and Chief Science Officer at AvroBio, a clinical - stage, gene therapy company based in Cambridge, Massachusetts.

Before joining Hookipa in June 2016, Joern was CEO of NASDAQ - listed uniQure N.V, a company pioneering adeno - associated virus - based gene therapy.

In 1998 he co-founded Amsterdam Molecular Therapeutics (AMT; currently Uniqure), a gene therapy company that develops AAV - based gene therapy products.

Most recently, Dr. Gringeri was the Chief Operating Officer for Amsterdam Molecular Therapeutics (AMT), a Netherlands - based company engaged in human gene therapies for orphan diseases related to metabolic disorders, liver diseases, blood diseases, and disorders of the central and peripheral nervous systems.

Since the initial Michigan trial, the liposomal transport system — developed by researchers at Vical, a San Diego - based biopharmaceutical company interested in gene therapy — has been altered in ways that are expected to make it safer, more effective and easier to administer.

«We look forward to helping the company realize the tremendous promise of its gene therapy platform, which has the potential to provide patients suffering from these severe eye diseases with treatments that offer life - long clinical benefits, potentially based on a one - time therapeutic administration.»

Alachua, Fla. - based AGTC is a clinical - stage biotechnology company that uses its proprietary gene therapy platform to develop products designed to transform the lives of patients with severe inherited orphan diseases in ophthalmology.