For example, if
we block mutant huntingtin production in cells or animals with «gene silencing» techniques, how can we confirm that this treatment actually does what it's supposed to do in the brains of patients with HD?
Not exact matches
Blocking nuclear export seemed to prevent cells from dying and counteracted the defects in neurons with
mutant Huntingtin, the researchers say.
the amino acid building
block that is repeated too many times at the beginning of the
mutant huntingtin protein