Sentences with phrase «breakthrough drug for»

The Patented Medicines Prices Review Board («Board») recently concluded a 7 year saga regarding its evaluation of the price for Soliris — Alexion's admittedly breakthrough drug for rare blood disorders.

«Just imagine if the next breakthrough drug for medication for heart disease or Alzheimer's of cancer is born right here in our borders,» said Astorino.

Not exact matches

But a breakthrough has yet to occur, simultaneously posing a financial conundrum for drug makers and a bitter pill for patients» caregivers.

But for all of the attention paid to its cancer drug pipeline, Bristol just scored a breakthrough therapy designation from the Food and Drug Administration for a treatment that targets hepatitidrug pipeline, Bristol just scored a breakthrough therapy designation from the Food and Drug Administration for a treatment that targets hepatitiDrug Administration for a treatment that targets hepatitis C.

In addition to the potential for medical breakthrough, most analysts who spoke with CNBC also noted that cancer drugs are not subject to increased political pressure to lower prices.

Coming off a year that saw a record number of new drug approvals, significant scientific breakthroughs and a year - end tax reform package that both significantly lowers corporate taxes and provides the long - awaited tax repatriation holiday, it's not surprising that biotech investors, executives and advisers were in a good mood as they gathered in San Francisco this year for the J.P. Morgan Healthcare Conference.

(Reuters)- Alnylam Pharmaceuticals Inc's RNAi - based drug that targets a rare genetic disease met the main goal of a key study, in a breakthrough for the new class of medicines that works by blocking disease - causing proteins.

AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, announced in July 2016 that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy Designation for the treatment based on preliminary clinical results from the trial of AVXS - 101.

Because so many of the patients in the early testing showed significant long - lasting responses, the study was continued and the FDA granted the drug «breakthrough therapy» status, allowing it to be fast - tracked for approval.

In a major breakthrough several years ago, two research groups, the Zuker group at Columbia and the Bachmanov group at the Monell Center for Chemical Senses, each got around this problem by finding drugs that could temporarily block a certain type of sodium channel in mice's mouths.

Scientists have made a major breakthrough in the global search for a new drug to beat the malaria parasite's growing resistance to first - defence treatments.

While researchers have long worked with nanoparticles for drug delivery, the findings put forth by He and his team represent a crucial breakthrough in addressing multidrug resistance in cancer cells.

Ocrelizumab was heralded as a breakthrough, and in March, the U.S. Food and Drug Administration approved it as a treatment for primary progressive and relapsing - remitting MS. Genentech now sells the drug as OcreDrug Administration approved it as a treatment for primary progressive and relapsing - remitting MS. Genentech now sells the drug as Ocredrug as Ocrevus.

«Hepatitis C: Life - threatening barriers in access to breakthrough drugs in US: First systematic study of Medicaid policies for hepatitis C treatment.»

«This is a major breakthrough for genetics studies on the virus and for designing ways to screen for effective drugs,» Rice says.

Researchers at McGill University have developed a new, low - cost method to build DNA nanotubes block by block — a breakthrough that could help pave the way for scaffolds made from DNA strands to be used in applications such as optical and electronic devices or smart drug - delivery systems.

On April 14 four finalists faced off at Stony Brook in front of the judges for this year's Discovery Prize, regaling the expert panel and a packed auditorium with rapid - fire speeches about breakthrough work on drug - resistant bacteria, the dynamics of subatomic particles, the origins of the universe and more.

Finding ways to use CaSR - directed drugs also for the treatment of diseases such as diabetes, Alzheimer's disease and various types of cancer, would be a breakthrough.

«This breakthrough could lead to more effective therapies for women with this very common subtype of breast cancer and be the therapeutic target that the drug companies have been waiting for.»

For example, Zykadia, a drug for metastatic lung cancer, received a «breakthrough therapy» designation that allows expedited approval based on preliminary evidence for certain drugs that treat serious conditioFor example, Zykadia, a drug for metastatic lung cancer, received a «breakthrough therapy» designation that allows expedited approval based on preliminary evidence for certain drugs that treat serious conditiofor metastatic lung cancer, received a «breakthrough therapy» designation that allows expedited approval based on preliminary evidence for certain drugs that treat serious conditiofor certain drugs that treat serious conditions.

In July 2014, the U.S. Food and Drug Administration granted CTL019 its Breakthrough Therapy designation for the treatment of relapsed and refractory adult and pediatric ALL, a step which is intended to expedite the development and review of new medicines that treat serious or life - threatening conditions, if a therapy has demonstrated substantial advantages over available treatments.

«Expedited approaches can be used without compromising efficacy standards for drugs that demonstrate breakthrough therapy potential.»

Taking that concept into biomedical research has yielded a breakthrough: This past May the mTOR inhibitor everolimus was approved by the U.S. Food and Drug Administration for the treatment of advanced pNET, the first drug in this class approved for this diseDrug Administration for the treatment of advanced pNET, the first drug in this class approved for this disedrug in this class approved for this disease.

«Breakthrough in live - cell imaging studies could lead to innovative drugs for a variety of human diseases.»

In the late 1990s beta - blockers, drugs commonly given to patients to reduce blood pressure, were hailed as a breakthrough for reducing life - threatening post-surgical cardiac complications in high - risk surgical patients as a result of two small high - profile randomized studies.

For example, Novartis and the University of Pennsylvania's lead candidate (CTL019) for treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical needs (For example, Novartis and the University of Pennsylvania's lead candidate (CTL019) for treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical needs (for treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical needs Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical needs drug development pathway for high unmet medical needs (for high unmet medical needs (1).

This despite a plethora of basic research breakthroughs abroad that made SMA ripe for drug development.

Chicago, Ill., July 20, 2016 — AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, today announced the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy Designation for AVXS - 101, the company's lead development candidate for the treatment of spinal muscular atrophy (SMA) Type 1 in pediatric patients.

Those breakthroughs include the development of new screening methods to search for effective drugs, new ways to treat hepatitis B using different approaches to shut down the virus, a new blood biomarker that aids in the early detection of liver cancer, and a promising drug that selectively kills liver cancer cells in animal studies.

For example, Novartis and the University of Pennsylvania's lead candidate (CTL019) for treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical neeFor example, Novartis and the University of Pennsylvania's lead candidate (CTL019) for treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical neefor treating a range of hematological malignancies received breakthrough status from the US Food and Drug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical neDrug Administration (FDA) in 2014, permitting access to an expedited drug development pathway for high unmet medical nedrug development pathway for high unmet medical neefor high unmet medical needs.

Arthritis, What Exercises Work: Breakthrough Relief For The Rest Of Your Life, Even After Drugs & Surgery Have Failed by Dava Sobel has the right exercises for your kind of arthritis, pain - level, age, occupation, and hobbiFor The Rest Of Your Life, Even After Drugs & Surgery Have Failed by Dava Sobel has the right exercises for your kind of arthritis, pain - level, age, occupation, and hobbifor your kind of arthritis, pain - level, age, occupation, and hobbies.

A breakthrough film for director Gus Van Sant (Good Will Hunting, Psycho), Drugstore Cowboy followed the exploits of a group of junkies that got their fixes from the catches they'd get after robbing local pharmacies and hospitals of their prescription drugs.

Aging populations, new breakthroughs in drugs, and increasing health care coverage all indicate that demand will be growing for the foreseeable future.

History also teaches us the greatest advances in medicine have come from scientific breakthroughs, whether the discovery of antibiotics, or improved public health practices, vaccines for smallpox and polio and many other infectious diseases, antiretroviral drugs that can return AIDS patients to productive lives, pills that can control certain types of blood cancers, so many others.

With different vehicles, medical breakthroughs, and access to new drugs and technology, a visitor to the U.S. might be more safely covered in case of emergency than a visitor to another foreign country because the U.S. provides the same level of medical care for its citizens, as it does for its visitors.

About Blog Seven Bridges is the biomedical data analysis company accelerating breakthroughs in genomics research for cancer, drug development and precision medicine.

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