Sentences with phrase «breakthrough for treatment»
We're taking a big picture perspective across neuromuscular diseases to uncover breakthroughs for treatments and cures.
https://www.mda.org/ Not exact matches
«If we determine that our [treatment] can prevent or delay the onset of symptoms in healthy yet high - risk populations, this would represent a tremendous breakthrough for those that may face this debilitating disease.»
But for all of the attention paid to its cancer drug pipeline, Bristol just scored a breakthrough therapy designation from the Food and Drug Administration for a treatment that targets hepatitis C.
On the other hand, the potential for profit is extraordinary if and when new treatment breakthroughs occur.
«In health care, patients sometimes want to donate tissue to scientific research that can help lead to medical breakthroughs, such as treatments and cures for serious diseases,» he writes on Planned Parenthood's website.
Cincinnati, Ohio USA About Blog Cincinnati Children's is a not - for - profit hospital and research center pioneering breakthrough treatments, providing outstanding family - centered patient care and training health care professionals for the future.
Founder & CEO of U.S. Water, Allan Bly, commented on the launch of new PhosZero ™, stating, «I am very proud of our scientists for developing this great breakthrough in sustainable treatment for cooling water.
An internationally recognized expert on the treatment of self - injury, she lectures extensively on the subject and is co-author of the book, Bodily Harm: The Breakthrough Healing Program for Self - Injurers as well as Self Injury: A Manual for School Professionals.
They claim they have the breadth of clinical experience and years of research, which have translated into scientific breakthroughs in the treatment of infertility, and ultimately offering the latest medical advances for patients along with the highest fertility success rates.
The breakthrough could open the floodgates for similar treatments for neurological conditions such as Huntington's, motor neurone disease and possibly even Alzheimer's.
AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, announced in July 2016 that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy Designation for the treatment based on preliminary clinical results from the trial of AVXS - 101.
Scientists have made a major breakthrough in the global search for a new drug to beat the malaria parasite's growing resistance to first - defence treatments.
«It is truly a breakthrough for advancing detection and treatment of brain injuries.»
Dr Lee Campbell, Research Projects and Science Communications Manager at Cancer Research Wales, who part - fund the study, commented: «This is an exciting breakthrough as cancer stem cells are thought to be responsible for the failure of many cancer treatments and the re-emergence of cancers, often many years after the initial disease.
Ocrelizumab was heralded as a breakthrough, and in March, the U.S. Food and Drug Administration approved it as a treatment for primary progressive and relapsing - remitting MS. Genentech now sells the drug as Ocrevus.
«Hepatitis C: Life - threatening barriers in access to breakthrough drugs in US: First systematic study of Medicaid policies for hepatitis C treatment.»
We hope this leads to the ability to design, study and test new therapies for every patient on their own cells in the lab, leading to new treatments and breakthroughs in personalized medicine for individuals with a variety of lung diseases, including cystic fibrosis,» explained lead author Katherine McCauley, a PhD student at BUSM.
Sengupta and his colleagues parlayed that balloon breakthrough into a new strategy for cancer treatment: a nanocell.
Dr. Alan S. Cross, Professor of Medicine at University of Maryland School of Medicine, who was not involved in the research, shared his input: «This is a major conceptual breakthrough in our understanding of infection and immune disease mechanisms and may have implications for novel approaches to the treatment of other diseases characterized by cytokine storm.
A breakthrough in understanding human skin cells offers a pathway for new anti-ageing treatments.
This breakthrough could lead to less invasive, and more controlled and selective immunotherapies for cancer treatment.
Finding ways to use CaSR - directed drugs also for the treatment of diseases such as diabetes, Alzheimer's disease and various types of cancer, would be a breakthrough.
The breakthrough treatment comes, however, at a price that may place it out of reach for all but the wealthiest or best - insured patients.
In July 2014, the U.S. Food and Drug Administration granted CTL019 its Breakthrough Therapy designation for the treatment of relapsed and refractory adult and pediatric ALL, a step which is intended to expedite the development and review of new medicines that treat serious or life - threatening conditions, if a therapy has demonstrated substantial advantages over available treatments.
In a major breakthrough for ovarian and uterine cancers, Yale researchers have defined the genetic landscape of rare, highly aggressive tumors called carcinosarcomas (CSs), pointing the way to possible new treatments.
He noted that the panel played a big role in shepherding into law a 2012 measure — the FDA Safety and Innovation Act (FDASIA)-- which created a new «breakthrough therapy» designation to speed the approval process for certain treatments for seriously ill patients.
The potential is there for the wastewater treatment sector to exploit this breakthrough, which other teams in Europe have made in parallel with us.
The study can be regarded as a breakthrough, as the results change our understanding of the pathogenesis of AMD and also open new avenues for the treatment of the dry form of AMD.
Taking that concept into biomedical research has yielded a breakthrough: This past May the mTOR inhibitor everolimus was approved by the U.S. Food and Drug Administration for the treatment of advanced pNET, the first drug in this class approved for this disease.
Thanks to a breakthrough led by researchers in the Cockrell School of Engineering at The University of Texas at Austin, treatment for hemophilia can now be administered via a biodegradable system, a capsule, giving people affected by the hereditary bleeding disorder hope for a less expensive, less painful treatment option than conventional injections or infusions.
Introduced in 1992, ICSI was widely regarded as a breakthrough in the treatment of male infertility, which is the problem for an estimated 40 per cent of infertile couples.
Charles Akle, Chairman of Immodulon, said: «The results from this study are remarkable and represent a significant breakthrough in the development of immunotherapy for the treatment of pancreatic cancer.
Researchers have developed the first animal model simulating the eye complications associated with the thyroid condition Graves» disease, a breakthrough that could pave the way for better treatments, according to a recent study accepted for publication in The Endocrine Society's journal Endocrinology.
The Company's potential breakthrough treatment for high - risk type 1 diabetes, called PEC - DirectTM is expected to begin clinical trials early next year.
Associated Press «For all the excitement, big questions remain about how to turn thisweek's stem - cell breakthrough into new treatments for the siFor all the excitement, big questions remain about how to turn thisweek's stem - cell breakthrough into new treatments for the sifor the sick.
These breakthroughs may suggest new approaches for the treatment of malignant tumors.
New research with mice has revealed a major breakthrough in the use of cough medicine ingredient noscapine as a prophylactic treatment for prostate cancer.
Steve tells us how his interest in stem cells led him into cancer research, and the potential for breakthroughs in brain tumour research and treatment.
From the preventive vaccine for cervical cancer to the first therapy ever proven to extend the lives of patients with metastatic melanoma, immunology has already led to major treatment breakthroughs for a number of cancers.
Treatment for each child is individualized, combining the best available current knowledge with leading edge research breakthroughs, often involving world renowned researchers from right here at the University of Michigan.
The neurosurgeons at Penn Medicine's Center for Functional and Restorative Neurosurgery are leaders in breakthrough surgical treatments for patients with movement disorders including Parkinson's disease, tremor from multiple sclerosis or other causes, dystonia, and medically intractable epilepsy.
Diabetes Innovation 2012 will provide a powerful foundation for sustained advancement in all facets of diabetes prevention, treatment and payment reforms including social media and gaming, translational research breakthroughs, food sourcing, distribution to mobile patient technologies and everything in between.
The Company's pluripotent stem cell - derived islet cell replacement therapy, the PEC - Direct ™ product candidate, has the potential to be a breakthrough treatment for high - risk type 1 diabetes.
«These results indicate a treatment breakthrough for saving the vision of people with diabetic macular edema,» said Neil M. Bressler, M.D., chair of the DRCR.net and chief of the Retina Division at the Wilmer Eye Institute, Johns Hopkins University.
Chicago, Ill., July 20, 2016 — AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, today announced the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy Designation for AVXS - 101, the company's lead development candidate for the treatment of spinal muscular atrophy (SMA) Type 1 in pediatric patients.
There are at least 265 different genes in which mutations can cause blindness; breakthroughs in gene therapy are allowing scientists to develop treatments for diseases that were previously untreatable, giving hope to millions.
«Ontarians should be proud of this homegrown breakthrough that holds promise for providing new therapies and treatments for people with Duchenne muscular dystrophy.
Jill O'Donnell - Tormey, Ph.D., CRI chief executive officer and director of scientific affairs, was on hand to speak to the more than 250 attendees about breakthroughs in immunotherapy and CRI's role in bringing these new treatments to more patients sooner, and to thank the organizers and all in attendance for supporting this important work.
Successful cell therapy treatments for such afflictions will be not only significant medical breakthroughs, but also in very high demand.
Our talented team of scientists, scientific advisors, and board directors is working to accelerate breakthrough treatments for patients with significant unmet medical needs.