Evaluation and validation of
candidate gene products entail elucidation of their functional networks and mechanisms of action.
Not exact matches
Their favorite
candidate is a wheat
gene whose enzyme
product destroys the Cryphonectria acid that eats away at chestnut bark.
Most recently, she has led the planning and execution of a program for a new
gene therapy
product candidate, from ideation through proof - of - concept study, and mapping out the development plan.
There will be a rush of new research and development to pull in the most plausible
candidate genes: competition will drive this process, because specific genetic alterations will quickly become standardized, commoditized, widely cross-licensed
products.
AGTC's lead
product candidates focus on rare diseases of the eye, caused by mutations in single
genes, that significantly affect visual function and currently lack effective medical treatments.
AGTC plans to use the net proceeds of the offering to fund preclinical investigation and Phase 1/2 trials of potential
product candidates for treatment of wet AMD; to expand its manufacturing capabilities and create a pilot manufacturing group; to in - license, acquire or invest in complementary
gene therapy, technologies,
products or assets; and for working capital and other general corporate purposes.