Not exact matches
This study represents a significant step towards the development of clinical trials in
gene therapy for the
curative treatment of hereditary deafness and balance loss in humans.
For his part, Collins, who has led NIH since 2009 and been kept on by the Trump administration, pointed to an array of promising NIH activities, including the development of new technologies to provide insights into human brain circuitry and function through the Brain Research through Advancing Innovative Neuroethologies (BRAIN initiative) and the use of the
gene - editing tool CRISPR - Cas9 to correct mutations and clear the way to develop and test a «
curative therapy» for the first molecular disease: sickle cell disease.
«While each of these
genes was independently associated with metastatic prostate cancer, they have never been studied together in the context of early detection of patients with prostate cancer that will relapse after localized therapy with
curative intent, «according to the authors, led by Leigh Ellis, PhD, in the Dana - Farber Department of Oncologic Pathology.
But until
gene therapy is more commonplace, the only
curative treatment for sickle cell is hematopoietic stem cell transplantation.