Sentences with phrase «cures haemophilia»
Ohmori, Tsukasa, et al. «CRISPR / Cas9 - mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice.»
http://blog.addgene.org/
Cellectis, the French genome engineering specialist, and VIB together conduct research into new approaches to cure haemophilia.
Not exact matches
Clotting - factor infusions treat symptoms of haemophilia, but gene therapy could provide a cure.
Shire CEO Flemming Ornskov - who has a large conventional haemophilia business and is also chasing Biomarin and Spark in hunting a cure for the bleeding disorder - sees both the opportunities and the difficulties of gene therapy.
Repairing the faulty genes that cause haemophilia could ultimately cure the disease, but it will be a tough challenge
A «cure» for haemophilia is one step closer, following results published in the New England Journal of Medcine of a groundbreaking gene therapy trial led by the NHS in London.