This cured the mice of the hereditary
disease tyrosinemia, which causes the amino acid tyrosine to accumulate and can lead to liver failure.
Not exact matches
In a study of mice, they found that they could correct the mutated gene that causes a rare liver disorder, in 6 percent of liver cells — enough to cure the mice of the
disease, known as
tyrosinemia.
«This finding really excites us because it makes us think that this is a gene repair system that could be used to treat a range of
diseases — not just
tyrosinemia but others as well,» says Daniel Anderson, associate professor in MIT's Department of Chemical Engineering and a member of MIT's Koch Institute for Integrative Cancer Research and Institute for Medical Engineering and Science (IMES).