Sentences with phrase «enzyme replacement»

Treatment varies depending on the severity of symptoms, but often includes enzyme replacement therapy.

His practice covers various technological areas such as enzyme replacement therapies, vaccines, therapeutic antibodies, metabolic engineering and drug delivery.

Dog yellow diarrhea can also be due other causes such as medications such as those used for pancreatic enzyme replacement therapy and a virus such as parvo.

Pompe is a neuromuscular disease that can ultimately be fatal, even with enzyme replacement therapy.

Wiberg et al studied the effect of long term enzyme replacement treatment in 76 German Shepherd Dogs or Rough Coated Collies with EPI.

His current research interests include the development of enzyme replacement therapy for metabolic storage disorders other than Gaucher disease, as well as gene therapy for these conditions.

Pancreatic enzyme replacements come in powder, capsule, or tablet form.

As each of the subsequent and different enzyme replacement therapies targeting distinct MPS diseases sought FDA approval, the clinical trial requirements increased substantially.

Amicus has a drug in phase 2 trials that leverages their advanced enzyme replacement chaperone platform.

Brineura, a biweekly enzyme replacement therapy produced by BioMarin Pharmaceutical, delays the loss of walking in individuals with a rare genetic disorder.

While enzyme replacement therapy can correct the deficiency in peripheral tissues, researchers have been unable to channel the enzyme across the so - called blood - brain barrier to prevent the accumulation of glucocerebroside in the brain, which results in neuronal degeneration.

A number of treatments exist, including enzyme replacement therapy and hematopoietic stem cell transplantation, but efficacy depends upon diagnosing the disease and its specific form as early as possible.

However, the lack of antibacterial pancreatic secretions and the presence of undigested food seem logical reasons for SIBO to develop, and the requirement for antibiotics in some patients with EPI before an optimal response to enzyme replacement support the idea of secondary SIBO.

Experimentally, gene therapy, bone marrow transplants and enzyme replacement seem to have helped some.

Enzyme replacements usually result in improvement of the clinical signs, and dietary management.

Patients who have lysosome diseases like mucolipidosis can be treated with enzyme replacement therapy.

EPI is diagnosed based on blood tests and is managed with pancreatic enzyme replacements and dietary management, which usually improve clinical signs.

Hallal had justified Alexion's $ 8.4 billion purchase of Synageva Biopharma in 2015 by touting the blockbuster potential of enzyme replacement therapies Kanuma and SBC - 103.

«In our study, we used a gene therapeutic approach, but you could purify the modified protein and inject it intravenously just like it is already done for enzyme replacement therapy,» explains Spencer.

In 2015, we got our first exclusive contract with a pharmaceutical company that makes an enzyme replacement therapy for hypophosphatasia, which is a genetic bone disease where babies are born without this specific enzyme.

Glycomine will use the proceeds from this financing to complete IND enabling pre-clinical studies and initiate clinical studies of its substrate replacement therapy in patients with Congenital Disorder of Glycosylation Type Ia (CDG - Ia), and to accelerate discovery efforts towards an enzyme replacement therapy for N - glycanase deficiency (Ngly1).

This year, Alexion anticipates U.S. approval for Strensiq, an enzyme replacement therapy for HPP.

Now that the cause of the symptoms is known, it is possible to think about an enzyme replacement therapy for the patients.

Week after week, Wang saw families bringing their children in for enzyme replacement therapy to treat a group of rare metabolic diseases called mucopolysaccharidoses (MPS).

• 2004 - 2005 (Ospedale Maggiore): «Alpha dystroglican glycosilation in patients affected with congenital muscular dystrophy» • 2006 (Ospedale Maggiore): Characterization of the FSHD animal model • 2008 - 2012 (Telethon): «Genetic Biobank Network» • 2008 - 2010 (Telethon): «Italian clinical network for the FSHD» • 2009 - 2012 Coordinator of the Italian study: Acid Maltase Deficiency and Enzyme Replacement Therapy

Pancreatic enzyme replacement — to help break food down into smaller, more absorbable nutrients

Schneider MU, Knoll - Ruzicka ML, Domschke S, Heptner G, Domschke W. Pancreatic enzyme replacement therapy: comparative effects of conventional and enteric - coated microspheric pancreatin and acid - stable fungal enzyme preparations on steatorrhea in chronic pancreatitis.

Treatment includes a change to a lower fat diet such as Hills Prescription Diet i / d and enzyme replacement therapy.

EPIPRO ™ is specifically formulated for enzyme replacement therapy and has the required enzyme levels to be effective.

Treatment includes supplementation with enzyme replacements.

However, if cost is a really important factor, the dog food is much less important than the enzyme replacement therapy, whichever one you use.

We got EPI confirmation from our vet and placed her on Pancreatic Enzyme replacement.

EPI is diagnosed based on blood tests and is treated with pancreatic enzyme replacements.

The treatment of EPI often includes the recommendation of an enzyme replacement.

The enzyme replacement often comes as a powder to be mixed with your dog's food at each meal.

Roger did God's work with Allie, giving her an enzyme replacement supplement that supplies the digestive system with the missing enzymes, and encouraging Allie to resume eating once again.

Enzyme replacement therapy for mucopolysaccharidosis VI: growth and pubertal development in patients treated with recombinant human N - acetylgalactosamine 4 - sulfatase