Sentences with phrase «fatal lysosomal storage»
The drug candidate is intended for the treatment of subjects with neuronal ceroid lipofuscinosis, aka Batten Disease, a fatal lysosomal storage disease that primarily affects the nervous system in children.
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Dr. Jim ’83 and Anne ’80 Gardner, who own Gardner Animal Hospital in Eufaula, learned through social media about the lifesaving research being conducted at the college's Scott - Ritchey Research Center for GM1 gandliosidosis, a lysosomal storage disease that attacks the brain and spinal cord, and is a progressive and degenerative condition that is always fatal in children.