Sentences with phrase «field of gene therapy»
UniQure's entrance to the public market is also a major show of faith in the nascent field of gene therapy, which has been growing steadily in recent years.
inc.com
THE BELEAGUERED field of gene therapy has received a boost from a promising new DNA treatment for the most common form of haemophilia.
Her game - changing technology takes a mysterious bacterial genetic code and transforms it into a powerful tool for cutting and pasting bits of genetic material — meaning not only could the entire field of gene therapy be revived, but her genome - editing tool could one day be used to treat a range of diseases, from cancer and AIDS to hereditary disorders like Down syndrome and Huntington disease.
«Today's approval marks another first in the field of gene therapy — both in how the therapy works and in expanding the use of gene therapy beyond the treatment of cancer to the treatment of vision loss — and this milestone reinforces the potential of this breakthrough approach in treating a wide - range of challenging diseases,» FDA Commissioner Scott Gottlieb said in a statement.
The very virus that may have killed Jesse Gelsinger and temporarily cratered the field of gene therapy is now being recruited to help cure terminal cancer patients.
«Today's approval marks another first in the field of gene therapy — both in how the therapy works and in expanding the use of gene therapy beyond the treatment of cancer to the treatment of vision loss — and this milestone reinforces the potential of this breakthrough approach in treating a wide - range of challenging diseases,» FDA Commissioner Scott Gottlieb said in a statement.
The LCA2 trials are a rare success for the field of gene therapy, which has also cured children with the immune disorder known as bubble boy disease.
The success is a much - needed shot in the arm to the field of gene therapy, which has recently struggled with safety concerns.
The announcement last month that a fifth child who received gene therapy for an immune system disease has developed leukemia was the latest blow to the field of gene therapy.
Thereafter, I received postdoctoral training at the University of Michigan in Ann Arbor in the field of gene therapy, under the mentorship of Dr. Jeffrey Chamberlain, a leading expert in the field of gene therapy for Duchenne muscular dystrophy.
Prof. Ritter has over 20 year experience in the field of gene therapy in organ transplantation.
The experts aligned on this project are among the top in the field of gene therapy.