Sentences with phrase «first gene therapy trial»

The 1990s saw extreme advances in technology, with the World Wide Web, the first gene therapy trial, and the first designer babies [8] all emerging in 1990 and being improved and built upon throughout the decade.

Researchers say they see promising results from the first gene therapy trial for Alzheimer's disease.

IN TWO months» time, a group of profoundly deaf people could be able to hear again, thanks to the world's first gene therapy trial for deafness.

The patient was the first in a gene therapy trial to die of the therapy itself; his death is the latest blow to a field that has been struggling to live up to the promise and hype surrounding the first gene therapy trials a decade ago.

The first gene therapy trials were carried out in 1990 treating a four - year old patient who suffered from severe combined immunodeficiency (SCID)(1).

Not exact matches

A U.K. team is designing a clinical trial even more radical than prenatal stem cell therapy: the first ever test of gene therapy in pregnancy.

«First trial of gene therapy for cystic fibrosis to show beneficial effect on lung function.»

Although several experimental trials of gene therapy are under way, some of them for more than a decade, uniQure is the first in the West to win regulatory approval for a commercial treatment.

Women were not included in the first trial of gene therapy, which was mainly concerned with proving the safety of the technique.

WOMEN with cystic fibrosis are to join British gene therapy trials for the first time.

The «transformational» results have particular significance as the first successful gene therapy trial for the haemophilia A.

It is the first time that a gene therapy based on genetically modified stem cells is tested in a multicenter, international clinical trial that shows a reproducible and robust therapeutic effect in different centers and different countries.

Researchers reported promising preliminary outcomes for the first four children enrolled in a U.S. gene therapy trial for Wiskott - Aldrich syndrome (WAS), a life - threatening genetic blood and immune disorder, at the 57th annual meeting of the American Society of Hematology.

Within the past 10 years or so, lentiviruses have shown promise in clinical trials (1 — 3), and adenoassociated viruses (AAVs) have been used in the first approved gene therapies in the Western world (4).

Weill Cornell is the birthplace of many medical advances — including the development of the Pap test for cervical cancer, the synthesis of penicillin, the first successful embryo - biopsy pregnancy and birth in the U.S., the first clinical trial of gene therapy for Parkinson's disease, and most recently, the world's first successful use of deep brain stimulation to treat a minimally conscious brain - injured patient.

CRISPR Therapeutics is pioneering a new class of medicines, to conduct the first company - sponsored clinical trial of a CRISPR gene - edited therapy.

Gene therapy remains experimental 20 years after its first human trials because of a series of vexing problems.

CAR T - cell Therapy: Scott McIntyre's Story After many treatments for his B - cell lymphoma failed, Scott McIntyre became the first UChicago Medicine patient to undergo CAR T - cell gene therapy in a clinicalTherapy: Scott McIntyre's Story After many treatments for his B - cell lymphoma failed, Scott McIntyre became the first UChicago Medicine patient to undergo CAR T - cell gene therapy in a clinicaltherapy in a clinical trial.

Indeed, Leber Congenital Amaurosis (LCA) was one of the first recessive disorders to undergo clinical trials for gene replacement therapy.

The treatment, developed at the University of Pennsylvania with clinical trials carried out at Children's Hospital of Philadelphia and the University of Iowa, is the first time gene therapy is used to treat an inherited disease and could lead to treatments of other currently untreatable conditions.

The results from the first human trials for a gene therapy to treat haemophilia A have just been published.