Sentences with phrase «for blood disorders»
The trial stemmed from a decade - long collaboration between St. Jude and University College London to discover effective gene therapies for this blood disorder.
stjude.org
«These are remarkable data,» says Amit Nathwani at University College London, who is using AAVs in potential treatments for a blood disorder called haemophilia B. «Liver fibrosis is a major clinical problem and if these data can be reproduced clinically, the National Health Service would save billions and patients would be given a new lease of life.»
Corn's dream might not be far off, at least for blood disorders such as sickle cell disease.
Spark Therapeutics» stock soared 20 % in Wednesday trading on the heels of its second quarter 2017 earnings report and some (very) early data on the gene therapy - focused firm's treatment for the blood disorder hemophilia A.
-- You are currently taking medications for a blood disorder (such as blood thinners).
From Andy Gluss's perspective, weekly blood tests and regular transfusions for a blood disorder qualify him as a «frequent flyer» in Norris Cotton Cancer Center's Hematology unit.
EHA Task Force on Fair Pricing: a new economic model is needed to make the right treatment available for every blood disorder - no matter how rare - across Europe and at a price that is fair to patients, manufacturers and tax payers.
He earned his Ph.D at McMaster University in Hamilton, Canada, where he developed new gene therapy strategies for blood disorders.
One early form of CRISPR - based gene therapy could involve editing the genes responsible for blood disorders like sickle - cell anemia in bone marrow cells, growing them into mature blood cells and injecting them back into patients.
As the principal regulator of iron, hepcidin has become a target for researchers developing novel therapies for blood disorders.
Along with his colleagues, Shaqfeh has now created the first simplified computer model of the process that forms that layer — a model that could help to improve the design of artificial platelets and medical treatments for trauma injuries and for blood disorders such as sickle cell anemia and malaria.
«To turn the new gene editing approach into a therapy for blood disorders, the British - 198 mutation would have to be introduced into blood - forming stem cells from the patient,» says Professor Crossley.
Renowned for our research and therapies for blood disorders, Texas Children's Hematology Center physicians conducts state - of - the - art clinical and scientific research aimed at understanding, preventing and curing blood diseases.
Dr. Sadelain has made major contributions to the generation and optimization of CAR T cells to treat cancer, as well as the development of stem cell therapies for blood disorders.