Sentences with phrase «for mucopolysaccharidosis»
Enzyme replacement therapy for mucopolysaccharidosis VI: growth and pubertal development in patients treated with recombinant human N - acetylgalactosamine 4 - sulfatase
http://bmjopen.bmj.com/
In addition, a trial for Mucopolysaccharidosis type I (MPS - I) is planned to start in 2018.
Researchers at the Biophysics Department of the Federal University of São Paulo (UNIFESP) in Brazil are developing a gene therapy for mucopolysaccharidosis type I...
Not exact matches
Clinical research activities are focused on the implementation of experimental protocols based on gene or cell therapy for the treatment of genetic blood disorders such as ADA - SCID, Wiskott - Aldrich Syndrome, Metachromatic Leukodystrophy, Beta - thalassemia, Chronic granulomatous disease, Mucopolysaccharidosis Type I (Hurler).