Scientists at the Whitehead Institute used CRISPR /
Cas9 gene editing method to restore activity to the fragile X syndrome gene in affected neurons.
UT Southwestern Medical Center researchers successfully used a
new gene editing method to correct a mutation that leads to Duchenne muscular dystrophy (DMD) in a mouse model of the condition.
There has been much excitement among scientists about the power of these new
gene editing methods, and particularly about the CRISPR / Cas9 system, which is relatively simple to use and generally very efficient.