Sentences with phrase «gene therapy»

And because each cell has its own unique set of mutations, we can not solve them with the methods of gene therapy in the adult organism either today or tomorrow.

I think, it's very promising approach in gene therapy, which eventually will enter the market.

In the future, scientists may be able to modify human stem cell lines in the laboratory by using gene therapy or other techniques to overcome this immune rejection.

It was one of only a handful of successful gene therapy trials in people.

And in an ironic twist, the work could yield a new way to treat common ailments such as heart disease and cancer with gene therapies.

But such gene therapy approaches in humans are notoriously difficult.

The potential applications for this technology include research on gene therapy treatments.

It's up to the scientific community to maintain and enforce international codes of ethics regarding clinical research on gene therapy techniques, the authors say.

Furthermore, the same technologies used to create genetic models of cancer show promise as gene therapies capable of repairing mutations that lead to a range of diseases.

A virus that has shown promise as a vector for human gene therapy causes liver tumors in neonatal mice.

The results suggest caution when interpreting data from molecular biological studies or developing gene therapies to treat various diseases.

DNA - based gene therapy products have been in clinical development since the 1990s.

The climate for gene therapy research has since begun a slow rebound.

Almost 10,000 human adults have already had their genes altered through gene therapy techniques used to treat genetic diseases.

Thus far, targeted gene therapy successes have been very limited.

The newest gene therapies work on mice, rats, and dogs with no apparent adverse effects.

The first diseases which benefited from gene therapy are rare genetic diseases in which the gene responsible had been identified, specifically severe immune deficiencies.

So that almost all diseases could be treated by gene therapy eventually.

Many researchers in the past used the traditional gene therapy technique to treat mitochondrial disorders.

A problem confronting gene therapy researchers is that they can not deliver enough beneficial genes to the precise location in the body where they are needed.

Such long - term expression is important for gene therapy studies in humans.

Approved treatments included gene therapies and the first new drugs for rare diseases in many years.

The lack of discrimination in the viruses used to carry therapeutic genes has been a major obstacle to testing gene therapy in humans.

This orderly structure falls apart in the mutant mice (middle column), but is dramatically restored after gene therapy treatment.

This is the first successful gene therapy treatment to halt a fatal brain disease.

He volunteered for experimental gene therapy to correct it.

But he contends that other gene therapies already in clinical trials suggest that the treatment could work.

One promising area of research involves gene therapy experiments.

In most previous in vivo gene therapy experiments, researchers have used viruses to carry the DNA into the patient's tissues.

How close are we to developing an effective gene therapy for treating cancer?

Our current platform is just the beginning of a continuum of investment in next generation gene therapy technologies and capabilities.

No one has followed gene therapy patients that long.

One caveat is that the mice were treated right after birth; hearing and balance were not restored when gene therapy was delayed 10 - 12 days.

Functional magnetic resonance imaging showed regions of their visual cortex lighting up that had been offline before gene therapy began.

This type of treatment is what we call gene therapy and researchers have been working on developing techniques to accomplish this for many years.

But gene therapy also needs to be carefully done and, ideally, two independent gene - manipulation systems would be used to ensure that stem cells remain firmly in control of clinicians.

In - the - body gene therapies often take advantage of the natural tendency of viruses to infect certain organs.

The finding could lead to studies of a similar gene therapy to treat people with inherited blood disorders.

The eye may be a particularly receptive place for gene therapy because it is a relatively contained space that does not mount a large immune response.

And gene therapy offers an elusive promise of fixing fundamental defects in our DNA.

Following gene therapy, levels of T, B and natural killer cells rose to near normal levels in five of the first six patients who enrolled in the study.

In most gene therapy studies, a «normal» gene is inserted into the genome to replace an «abnormal,» disease - causing gene.

Never has it been so easy to look up a circuit diagram, learn about gene therapy or read the latest papers about black holes.

These days, thanks to advances in virus technology, new gene therapy startups are popping up at a rapid clip.

Since then, however, researchers have continued to cautiously pursue gene therapy for certain disorders with known genetic origins.