Sentences with phrase «gene therapy company»

AveXis, Inc., a clinical - stage gene therapy company developing treatments for patients suffering from rare and life - threatening neurological genetic diseases, announced in July 2016 that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy Designation for the treatment based on preliminary clinical results from the trial of AVXS - 101.
• Nightstar Therapeutics, a London - based gene therapy company focused on retinal diseases, set the terms of its IPO.
• Krystal Biotech, a Pittsburgh, Penn. - based gene therapy company focused on dermatological diseases, filed for an IPO Monday.
LHV is co-founder, shareholder, member of the Scientific Advisory Board, and consultant of GenSight Biologics, an ophthalmology gene therapy company.
• LogicBio Therapeutics, a Foster City, Calif. - based gene therapy company, raised $ 45 million in Series B funding.
As a student, Arman did consultancy work for a friend who was launching a gene therapy company called Eos Neuroscience.
But gene therapy companies - which also include Bluebird Bio, BioMarin, Sangamo and GenSight - may need new business models.
Chris Mason is a Co-Founder and Chief Science Officer at AvroBio, a clinical - stage, gene therapy company based in Cambridge, Massachusetts.
In 1998 he co-founded Amsterdam Molecular Therapeutics (AMT; currently Uniqure), a gene therapy company that develops AAV - based gene therapy products.
Voyager Therapeutics, Inc., a clinical - stage gene therapy company, and AbbVie, a global biopharmaceutical company, announced that they have entered into an exclusive strategic collaboration and option agreement to develop and commercialize vectorized antibodies directed against tau for the treatment of Alzheimer's disease and other neurodegenerative diseases.
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