Sentences with phrase «gene therapy research by»

The policy — in the form of first Office Actions on a series of applications for patents on expressed sequence tags, ESTs — could greatly complicate basic gene therapy research by substantially allowing patents for small sequences of a gene that may later be used by the patent holder to corner ownership and uses of entire genes.

Not exact matches

Kevin Whittlesey (2006 - 07 Congressional Fellow sponsored by Optical Society of America and Materials Research Society) has moved into the gene therapy field at 4D Molecular Therapeutics as director of program and alliance management.

As Saaïd Safieddine, CNRS Director of Research at the Institut Pasteur and co-senior author of the study with Prof. Christine Petit (head of the Genetics & physiology hearing unit at the Institut Pasteur), explains, «we have just shown that it is possible to partially correct a specific form of hereditary hearing loss accompanied by balance problems using local gene therapy performed after the embryogenesis of the ear, which is primarily affected by the mutation responsible for the disorder.

In science news around the world, NASA's Cassini mission is about to take its final plunge into the atmosphere of Saturn after 13 years providing an unprecedented view of the planet and its moons, a fight over whether to preserve or develop of one Europe's oldest gold mining sites heats up again, the U.S. Food and Drug Administration approves the first cancer gene therapy for people, a U.S. court gives a green light to a $ 1 billion lawsuit brought by the Guatemalan victims and survivors of mid — 20th century syphilis experiments by research institutions including Johns Hopkins University, and more.

For his part, Collins, who has led NIH since 2009 and been kept on by the Trump administration, pointed to an array of promising NIH activities, including the development of new technologies to provide insights into human brain circuitry and function through the Brain Research through Advancing Innovative Neuroethologies (BRAIN initiative) and the use of the gene - editing tool CRISPR - Cas9 to correct mutations and clear the way to develop and test a «curative therapy» for the first molecular disease: sickle cell disease.

Being able to acquire new technologies, as well as becoming more innovative internally by venturing into new research areas, such as stem cell and gene therapy research, have allowed Genzyme to maintain its edge.

Independent studies by Hortelano's group and other research teams in Germany and the United States have shown that this oral gene therapy does not activate the immune system.

Using cell cultures, the research team also found two ways to prevent the toxicity caused by alpha - synuclein: gene therapy that forced the neurons to make more TOM20 protein protected them from the alpha - synuclein; and a protein that was able to prevent alpha - synuclein from sticking to TOM20 prevented alpha - synuclein's harmful effects on mitochondria.

The researchers, including scientists from The Genome Institute at Washington University School of Medicine, presented the research titled, «Patient - derived xenograft study reveals endocrine therapy resistance of ER + breast cancer caused by distinct ESR1 gene aberrations.»

Secondly, this is the first research to demonstrate that the loss of hair cells and hearing can be curtailed in USH3 mice by clarin - 1 gene therapy.

Ip thinks his research could help humans with kidney failure, either by creating a more efficient dialysis machine or through gene therapy to enable humans to mimic the turtle and eliminate urea via the mouth.

This work was supported by the Max - Planck - Society, the German Research Council (DFG), the Excellence Cluster Cardiopulmonary System (ECCPS), the University of Giessen - Marburg Lung Center (UGMLC), the Cell and Gene Therapy Center (CGT) of the University of Frankfurt and the EY10540 grant to PAT.

As gene therapy and CRISPR / Cas9 - style gene editing research progresses, we can anticipate demand for services such as those provided by the Viral Vector Core.

PNP Therapeutics, Inc. — a company based on a gene - therapy technology developed by scientists at Southern Research Institute and the University of Alabama at Birmingham (UAB)-- has found an approach that has abolished otherwise unmanageable human cancers in preclinical rodent studies.

The present research provides a theoretical backbone for gene introduction research previously conducted by trial - and - error, and is expected to contribute to the elucidation of the molecular basis of DNA medicines and gene therapy, and to make them more efficient.

Hot on the heels of last weeks report of the successful use of gene therapy to treat the eye disease Leber's congenital amaurosis comes a report that scientists lead by Nathalie Cartier and Patrick Aubourg of the French National Institute for Health and Medical Research have combined gene therapy and stem cell medicine to successfully... Continue reading Gene therapy on the bgene therapy to treat the eye disease Leber's congenital amaurosis comes a report that scientists lead by Nathalie Cartier and Patrick Aubourg of the French National Institute for Health and Medical Research have combined gene therapy and stem cell medicine to successfully... Continue reading Gene therapy on the bgene therapy and stem cell medicine to successfully... Continue reading Gene therapy on the bGene therapy on the brain

EC was supported by the Else Kröner - Fresenius - Stiftung, the Excellence Cluster Cardiopulmonary System (DFG; Exc147 - 1), the German Centre for Cardiovascular Research (BMBF) and the LOEWE Center for Gene and Cell Therapy (Hessen, Germany).

Study using disabled form of HIV in gene therapy wins highest award from Clinical Research Forum; others cited for advances revealing damage caused by long - term cortisone shots to treat arthritic knees; and gene replacement therapy for infants with deadly neuromuscular disease

Prof Thomas Ritter, leader of research programme, was recruited by the National University of Ireland, Galway as a lecturer in Gene Therapy and Regenerative Medicine and assumed his position in March 2005.

By identifying and treating gene mutations in dogs, his research moves us closer to gene therapy that could one day be used to manage and prevent glaucoma in humans.

This latest development in gene therapy is the result of more than two decades of painstaking genetic research by Jean Bennett, MD, PhD, and Albert M. Maguire, M.D., both Professors of Ophthalmology and Co-directors of the Center for Advanced Retinal and Ocular Therapeutics at Penn Medicine.

Avalanche will build on gene therapy research conducted by Drs. Jay and Maureen Neitz of UW's department of ophthalmology.

Funding: This work was supported by the Alliance for Cancer Gene Therapy (R.H.V.), the Onyx and Breezy Foundation (K.U.S.), the Barry and Savannah Poodle Memorial Fund and the Mari Lowe Comparative Oncology Center (N.J.M.), the Immunobiology Program of the Abramson Cancer Center at the University of Pennsylvania (NIH grant P30 CA016520, R.H.V.), and the Oncology Research fund at the Veterinary Hospital of the University of Pennsylvania (K.U.S.).