Sentences with phrase «gene therapy trial published»

Not exact matches

A one - time intravenous infusion of the high dose of gene therapy extended the survival of patients with spinal muscular atrophy type 1 (SMA1) in a Phase 1 clinical trial, according to a study published in the New England Journal of Medicine.

As a new generation of gene therapy clinical trials shows promise to cure or halt the progression of several rare diseases, the time has come to explore ways to pay for the cutting edge treatments, a pediatric hematologist - oncologist from Dana - Farber / Boston Children's Cancer and Blood Disorders Center argues in a commentary published by the journal Science.

A «cure» for haemophilia is one step closer, following results published in the New England Journal of Medcine of a groundbreaking gene therapy trial led by the NHS in London.

The research, part of a phase I clinical trial to test the safety of the treatment, was published as a letter to the editor in The New England Journal of Medicine earlier this week and will be in the September issue of Human Gene Therapy.

Spark Therapeutics» gene therapy for patients with haemophilia has seen some early success in clinical trials, according to a report published yesterday.

George Church, a Harvard Medical School geneticist who published one of the early papers on the use of CRISPR on mammalian cells, pointed out that people in his field have been doing genetic modification for decades, and said there are already 2,000 gene therapy trials underway, none of which use CRISPR.

The results from the first human trials for a gene therapy to treat haemophilia A have just been published.

Lung Cancer Breakthrough A study published in the September, 1998 issue of Nature Medicine concerned a preliminary trial using gene therapy to treat lung cancer.