«Groundbreaking
gene therapy trial set to cure hemophilia.»
Not exact matches
Some on the panel suggested they were particularly sensitive about such concerns given that it was at UPenn in 1999 that a young man, Jessie Gelsinger, died in a
gene therapy trial,
setting the field back for years.
In the same week that the
trial was approved, the Medical Research Council announced that it was to
set up its own committee to oversee its work in
gene therapy.
Sadly only a few of these are associated with an sufficiently extensive
set of evidence such that responsible human
trials are an immediate possibility: myostatin knockout for muscle growth and telomerase
gene therapies to offset some of the declines of aging.