Sentences with phrase «good duchenne»
Not exact matches
These are the muscular dystrophies (among which are Duchenne and Becker); motor neuron diseases (including ALS and SMA); the peripheral nerve disorders (CMT and Friedreich's ataxia); inflammatory myopathies; disorders of the neuromuscular junction; metabolic diseases of muscle as well as other myopathies.
http://www.sciencemag.org/
«For a stem cell therapy for Duchenne to move forward, we must have a better understanding of the cells we are generating from human pluripotent stem cells compared to the muscle stem cells found naturally in the human body and during the development process.»
This conference will provide up to date clinical education, resources, materials and networking, supporting your ability to provide the very best care to your patients and families living with Duchenne.
The research was supported by grants from the Oppenheimer Foundation, the National Institutes of Health, the National Center for Research Resources and the Chinese Scholarship Council of Chemistry and Chemical Engineering, as well as funding from the Center for Duchenne Muscular Dystrophy at UCLA and the Broad Stem Cell Research Center.
The authors were able to correct mutations in several well - characterized genetic disorders, including: Duchenne Muscular Dystrophy, Achondroplasia, and MECP2 - duplication syndrome using cells derived from human patients.
Thank you to everyone who continues to support PPMD's Gene Therapy Initiative, as well as the generous support of Duchenne foundations: Team Joseph, Team Saij, The Fund for Pete's Sake, Rashad's family and the Nicholoff family.
PPMD and Capricor Therapeutics recently hosted a webinar to learn about the 12 - month results from Capricor's HOPE - Duchenne Clinical Trial, as well as the company's plans for the HOPE - 2 Clinical Trial.