Sentences with phrase «haemophilia treatment»

The therapy hoped to resolve some of the problems surrounding haemophilia treatment by exchanging the continual infusions for a single vector infusion that could permanently boost Factor IX expression.

«We think we can change the whole concept of haemophilia treatment,» Shima says.

The nanotechnology approach that is being tested for inhibitor control could also improve the haemophilia treatment that is now at the cutting edge of clinical research: gene therapy.

Pills made from lettuce leaves could help to prevent one of the most serious complications of haemophilia treatment

Although its launch in Britain last week could give them access to uncontaminated and potentially limitless supplies, the 95 haemophilia treatment centres may not be able to afford the new drug, which costs 52p per unit, compared with 20 to 45p for factor 8 extracted from human blood.

Existing haemophilia treatments tip the balance towards clotting by adding what the body lacks — the clotting factor that is missing or defective.

Not exact matches

Last week, Sanofi agreed to buy U.S. haemophilia specialist Bioverativ for $ 11.6 billion, its biggest deal for seven years and a major play to strengthen its presence in treatments for rare diseases.

Biopharmaceutical treatments, led by haemophilia, make up around 20 percent of Novo's sales, with diabetes and obesity products accounting for the remaining 80 percent.

«These are remarkable data,» says Amit Nathwani at University College London, who is using AAVs in potential treatments for a blood disorder called haemophilia B. «Liver fibrosis is a major clinical problem and if these data can be reproduced clinically, the National Health Service would save billions and patients would be given a new lease of life.»

Experiments in mice suggest that treatment of haemophilia could be more successful if the baby's immune system is primed while in the womb

Replacing the clotting ability lacking in haemophilia has been the treatment since the 1840s, when attempts were made to treat people with the disease by transfusion with whole blood from people with normal clotting.

We really now have the potential to transform care for people with haemophilia using a single treatment for people who at the moment must inject themselves as often as every other day.

Some concerns had been raised that by infusing patients with such a high activity gene, the treatment would overcorrect for haemophilia and give rise to thrombosis.

The treatment of haemophilia, dialysis and the medical applications of ultrasound are just a few historical examples.

iPS cells have been employed to generate cells for the treatment of various diseases including diabetes, cardiovascular disease, sickle cell anaemia, Parkinson's disease and haemophilia [19]--[23].

Psychosocial health and effective pain management are considered essential end points for optimal haemophilia care, but there is a significant gap in evidence - based treatments targeting these outcomes in people with haemophilia (PWH).