This discovery may trigger a reassessment in
hemophilia research.
Not exact matches
Most of this
research has centered on
hemophilia B, although
hemophilia A is five times as common.
Formerly a
research leader at CHOP, High pursued groundbreaking preclinical investigations in
hemophilia B gene therapy and provided scientific expertise to previous gene therapy trials in
hemophilia and other genetic disorders at CHOP before moving to Spark Therapeutics, which was spun off from CHOP in 2013.
«While an oral delivery platform will be beneficial to all
hemophilia B patients, patients in developing countries will benefit the most,» said Sarena Horava, the study's lead author who is a recent Ph.D. graduate from the Cockrell School's McKetta Department of Chemical Engineering and a National Science Foundation graduate
research fellow.
Sounds like science fiction, but new
research in an animal model of
hemophilia suggests that it can work - and now HD researchers are on the case.
Multiple
research groups and companies are hot on the tracks of unleashing CRISPR on sickle cell disease,
hemophilia, cystic fibrosis, Duchenne muscular dystrophy, genetic forms of blindness, and, of course, cancer.
We entered into an agreement with Bayer to
research, develop and commercialize AAV gene therapy products for treatment of
hemophilia A.
Dr. Brown's
research publications have included: Self - cutting and sexual risk among adolescents in intesive psychiatric treatment; Promoting safer sex among HIV - positive youth with
hemophilia: Theory, intervention, and outcome; Predictors of retention among HIV /
hemophilia health care professionals; Impact of sexual abuse on the HIV - risk - related behavior of adolescents in intensive psychiatric treatment; Heroin use in adolescents and young adults admitted for drug detoxification; and Children and adolescents living with HIV and AIDS: A review
Today academic institutions and teaching hospitals across the country receive federal or private grants to support groundbreaking
research using human fetal tissue on a wide range of conditions including diabetes, Parkinson's disease, Alzheimer's disease, spinal cord injuries,
hemophilia, leukemia, sickle cell anemia, cortical blindness, fetal aneuploidy, ALS, and others.