Sentences with phrase «new gene therapy»
These days, thanks to advances in virus technology, new gene therapy startups are popping up at a rapid clip.
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He earned his Ph.D at McMaster University in Hamilton, Canada, where he developed new gene therapy strategies for blood disorders.
«Efficacy of new gene therapy approach for toxin exposures shown in mouse study.»
Allowing some of the economic benefit derived from the Orphan Drug Act to be used to lower the price of new gene therapy drugs.
Celgene is working with Seattle - based Juno on an experimental new gene therapy designed to treat people with relapsed or refractory aggressive B - cell non-Hodgkin lymphoma.
The new Salk tool, called CasRx, opens up the vast potential of RNA and proteins to genetic engineering, giving researchers a powerful way to develop new gene therapies as well as investigate fundamental biological functions.
«What is truly remarkable about this revolutionary new gene therapy are the profound life - changing effects it offers patients with haemophilia.
«New gene therapy success in a rare disease of the immune system.»
Researchers at the University of Florida have developed a promising new gene therapy against multiple sclerosis (MS).
A Glaxo vet heads over to Genenta to help develop new gene therapy.
In a step toward accelerating the production of new gene therapies, scientists report in ACS Nano that they have developed remote - controlled, needle - like nanospears capable of piercing membrane walls and delivering DNA into selected cells.
The newest gene therapies work on mice, rats, and dogs with no apparent adverse effects.
A case in point: the new gene therapy for Leber congenital amaurosis, the eye disorder that causes progressive loss of vision, usually leading to complete blindness by age 40.
A new gene therapy treatment has restored some sight in a handful of blind patients suffering from Leber's congenital amaurosis, a syndrome in which, because of a broken or missing gene called RPE65, retinal photoreceptor cells malfunction and eventually die.
The unit is currently working on bringing to market a new gene therapy for the immune disease ADA - SCID, which is thought to affect only 350 children worldwide.
A new gene therapy developed by researchers at the University of Missouri School of Medicine has shown to protect mice from a life - threatening heart condition caused by muscular dystrophy.
The process of developing a new gene therapy treatment and securing FDA approval, they estimate, entails about eight years and direct costs of hundreds of millions of dollars.
Most recently, she has led the planning and execution of a program for a new gene therapy product candidate, from ideation through proof - of - concept study, and mapping out the development plan.
The new gene therapy drug will be available on Russian Federation pharmaceutical market in second quarter 2012 after the first batch certification process.
Researchers at the University of Florida have developed a new gene therapy that might help combat multiple sclerosis
Researchers at the University of Florida have developed a new gene therapy that shows promise in fighting multiple sclerosis (MS).
Yesterday a team of University of Pennsylvania researchers — led by Dr Pablo Tebas, Professor Carl June, and Dr Bruce Levine — announced the successful conclusion of a clinical trial to evaluate the safety of a new gene therapy technique for treating HIV.
New Orleans, LA (Scicasts)- Patients who had lost their sight to an inherited retinal disease could see well enough to navigate a maze after being treated with a new gene therapy, according to research presented today...
Carolyn's doctors were so impressed with her optimistic outlook that in 1995 they offered her an opportunity to participate in a test of a new gene therapy for breast cancer.