Sentences with phrase «nucleoside bypass»

Nucleoside bypass therapy is highly experimental and has never been used on someone with Charlie's rare mitochondrial disease, but it has also shown promise in some cases.

Specifically, they want their child to undergo nucleoside bypass therapy, a treatment that Cohen called «highly experimental» and which he noted would not work on all mitochondrial diseases.

Nucleoside bypass therapy, which was developed by Dr. Michio Hirano of Columbia University Medical Center, involves an oral dose of extra nucleosides that rebalances the concentration of these essential building blocks inside the mitochondria.

While the hospital advocates transitioning Charlie to end - of - life palliative care — officials have stated that «he has no quality of life and no real prospect of any quality of life» — his parents want him to undergo a highly experimental treatment in the United States called nucleoside bypass therapy.