Gelsinger had a rare liver disease and was
participating in gene therapy research at the university when he died.
Not exact matches
(
In the early 2000s, five children who participated in a retrovirus - based gene therapy trial for severe combined immunodeficiency developed leukemia
In the early 2000s, five children who
participated in a retrovirus - based gene therapy trial for severe combined immunodeficiency developed leukemia
in a retrovirus - based
gene therapy trial for severe combined immunodeficiency developed leukemia.)
Then came an invitation to
participate in a novel form of
gene therapy, one that could mark a first step toward a true cure for AIDS.
Donald Kohn of Children's Hospital
in Los Angeles, California, who is thinking about
participating, says he's optimistic that the safety issues will be solved and that
gene therapy will eventually become the standard of care.
We are part of a National Cancer Institute - funded Specialized Programs of Research Excellence (SPORE) grant and
participate in Children's Oncology Group and internal lymphoma studies within Texas Children's Cancer Center and the Cell and
Gene Therapy Program.
Using a disabled form of HIV to deliver the
gene therapy, researchers were able to halt the progression of the disease
in 15 out of 17 boys who
participated in the clinical trial.