Sentences with phrase «potentially therapeutic genes»
B's ability to deliver potentially therapeutic genes in disease models.
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«My team at Nationwide Children's has worked with commitment and dedication to develop a therapy that may subsequently be shown through future clinical trials to potentially alter the course of this unforgiving condition and provide a therapeutic option for the families and infants with SMA1,» says Jerry Mendell, MD, principal investigator in the Center for Gene Therapy at Nationwide Children's.
This technology helps researchers connect mutations in the so - called genomic «dark matter» with the genes they affect, potentially revealing new therapeutic targets for genetic disorders.
Previous studies have linked gene expression profiles in bCSCs with a clinical outcome [1, 2], and in this study the authors have extended this out to demonstrate that a DNA methylation profile may promote these changes, and furthermore, that this profile can be effectively used to predict prognosis, and potentially aid the therapeutic decision making.
To better understand UTIs and potentially offer new therapeutic strategies, a team of researchers analyzed 43 strains of E. coli sampled from 14 women with recurrent UTIs, and found that infection depends on both individual host susceptibility and how the bacteria express their genes.
«We look forward to helping the company realize the tremendous promise of its gene therapy platform, which has the potential to provide patients suffering from these severe eye diseases with treatments that offer life - long clinical benefits, potentially based on a one - time therapeutic administration.»