Several research groups are
pursuing gene therapy approaches to regenerate skin, such as using genes to control expression of growth factors involved in skin healing.
Not exact matches
Such a treatment might be combined with a
gene therapy approach, also being
pursued by her team and other groups, delivered directly to the brain to curtail mHTT expression.
Despite this new direction for identifying targets for pharmaceutical interventions against RP, the researchers underscore that
gene therapy still has great potential and possible benefits, and they are actively
pursuing efforts with this
approach for several forms of RP.
Pursuing such
gene -
therapy approaches offers a degree of bet hedging, says Herzog.
The track record of earlier
gene - editing
approaches suggests that the CRISPR companies
pursuing medical
therapies have a long road ahead.
The finding, published in the current issue of
Genes and Development1 represents a different
approach to cultivating specialized cells for transplant
therapy than that being
pursued in other labs.