That enzyme turned out to be defective in the short - lived strain of roundworms, but it worked fine in normal worms and in strains
rescued by gene therapy.
Not exact matches
Yet, their efforts to
rescue cone function
by gene therapy in mid-course LCA stages failed: when applied to 35 - day old Rpe65 - deficient mice,
gene therapy restores rod function only (Pang et al. 2010).
By targeting these cells with
gene therapy and virtual reality stimulation, we hope to
rescue them and prevent vision loss, perhaps even restore vision.