Sentences with phrase «successful gene therapy treatment»

This is the first successful gene therapy treatment to halt a fatal brain disease.

Led by Florian Eichler, MD, from Harvard Medical School and Massachusetts General Hospital, the study tested the first successful gene therapy treatment for cerebral adrenoleukodystrophy (ALD), a fatal degenerative brain disease that most severely affects boys.

Washington, D.C. — April 18, 2018 — The Clinical Research (CR) Forum, a non-profit membership association of top clinical research experts and thought leaders from the nation's leading academic health centers, today awarded its most prestigious honor to a Massachusetts General Hospital research team for its discovery of the first successful gene therapy treatment for a fatal brain disease, cerebral adrenoleukodystrophy (ALD).

Alain Fischer and Marina Cavazzana - Calvo announcing successful gene therapy treatment in April 2000.

The Jan. 12 issue of the journal Science provides an in - depth and timely review of the key developments that have led to several successful gene therapy treatments for patients with serious medical conditions.

Not exact matches

But he warns that gene therapy is still in its infancy worldwide and that even aside from the safety concerns, many technical problems must be solved before hopes of successful treatments can be raised.

Although gene therapy has since proved successful against rare diseases of the immune system and shown promise against AIDS (see «Genetic treatment closes door on HIV»), it has proved much harder to use it to treat CF.

Gene therapy is a very young field and has not yet resulted in any successful treatments.