Auburn University College of Veterinary Medicine, UMass Medical School to
test gene therapy treatment for Tay - Sachs and Sandhoff diseases Researchers at Auburn University College of Veterinary Medicine and UMass Medical School are nearing human clinical trials on a genetic therapy for two rare neurological diseases that are fatal to children.
Gene therapy: Généthon starts a clinical trial to
test a gene therapy treatment for a rare liver disease, Crigler - Najjar Syndrome
UC San Diego Health joins national clinical trial
testing a gene therapy treatment for individuals with hemophilia B.
Not exact matches
Just this year, over 50 U.S. genetics and
gene therapy startups raised at least $ 1 million to support genetics - based
treatments, including speeding trails, improving accuracy of
tests, and providing better platforms.
He and his lab, for example, along with the company Neurologix based in Fort Lee, N.J., are conducting a clinical trial to
test a similar
gene -
therapy treatment for Parkinson's disease.
These human
genes were also protective against alpha - synuclein - induced death, suggesting that they could be worth
testing as
gene therapy treatments for Parkinson's disease, Lu says.
The nanotechnology approach that is being
tested for inhibitor control could also improve the haemophilia
treatment that is now at the cutting edge of clinical research:
gene therapy.
The emergency
treatment would be the first
test of their
gene therapy approach over such a large and severely damaged area.
Reference materials are critical to properly evaluate the next - generation of
gene sequencing and genetic
testing methods that will increase the reliability and effectiveness of precision medicine (also known as «personalized medicine»), in which a person's genetic profile is used to create
treatments and
therapies unique to that individual.
The research, part of a phase I clinical trial to
test the safety of the
treatment, was published as a letter to the editor in The New England Journal of Medicine earlier this week and will be in the September issue of Human
Gene Therapy.
When
tested on mice that already had the disease, the
treatment significantly reversed the symptoms just eight days after the
gene therapy was delivered.
Inhaled
gene therapy for lung cancer could be a future
treatment if
tested properly.
Led by Florian Eichler, MD, from Harvard Medical School and Massachusetts General Hospital, the study
tested the first successful
gene therapy treatment for cerebral adrenoleukodystrophy (ALD), a fatal degenerative brain disease that most severely affects boys.
The
test measures the activity of
genes that control cell growth, and others that indicate a likely response to hormone
therapy treatment.
New
treatments are being
tested to tackle the crippling difficulties of vertigo, including a clinical trial of prosthetic ear implants and ear
gene therapy, with initial work revealing novel aspects of brain anatomy linked to balance which could be used as targets for future
treatments.