Immune cells from 4 - year - old Ashanti DeSilva are given working versions of the ADA gene to
treat severe combined immunodeficiency disorder (SCID).
Not exact matches
Fischer, in 2000, reported demonstrating the clinical efficacy of gene therapy for the first time, using blood stem cells to
treat a fatal genetic disorder called X-linked
severe combined immunodeficiency.
This was a virus - mediated therapeutic gene to
treat X-linked
severe combined immunodeficiency.
The first gene therapy trials were carried out in 1990
treating a four - year old patient who suffered from
severe combined immunodeficiency (SCID)(1).