Sentences with phrase «treat sickle cells»

St. Jude pioneered the use of hydroxyurea to treat sickle cells in children.

Emmaus Medical CEO Dr. Yutaka Niihara spent much of his career developing Endari, a recently approved FDA drug to treat sickle cell anemia.

Sydney McLeod kept up her studies at Success Academy Charter Schools despite extensive absences to treat her sickle cell anemia.

The researchers hope that the models could be used to evaluate drugs aimed at treating sickle cell crisis.

In animal models of disease, iPSCs have been used to treat sickle cell anemia, Parkinson's disease, diabetes, spinal cord injuries, and heart failure.

The findings, part of an upcoming paper, are a step toward treating sickle cell disease.

Not exact matches

So hold on tight, I'm gonna share EVERYTHING I've learned so far about cord blood with you... starting with this enlightening link on the general benefits... including the fact that «To date it can treat more than 80 diseases using Haematopoietic Stem Cell (HSC) transplants, including leukemia, sickle cell anemia, and metabolic disorders.&raCell (HSC) transplants, including leukemia, sickle cell anemia, and metabolic disorders.&racell anemia, and metabolic disorders.»

Either approach could produce enough HSCs to transplant and — pending further safety testing — potentially treat leukemia, sickle cell disease and other severe blood disorders.

In the early 1990s HemoTech was used in Zaire to successfully treat nine children with sickle - cell anemia.

Like Paizley Carwell - Bowen, Hina underwent transplantation at Children's Hospital of Los Angeles to treat her sickle - cell disease.

It's becoming possible to edit our genes to treat and prevent conditions like HIV and sickle cell disease or, more controversially, create designer babies

Patients with sickle cell trait received about 13 % more of the medications used to treat anemia than other patients to reach the same level of hemoglobin.

To assess risk, Thomas Adamkiewicz, codirector of the Hemoglobinopathy / Genomics Training Program at Morehouse School of Medicine in Atlanta, surveyed four medical centers and found that seven children with sickle - cell disease had been treated with umbilical cord blood from unrelated donors.

Gene editing techniques have the potential to treat blood disorders that run in families, such as thalassemia and sickle cell anemia, but their application has been largely limited to cells in a laboratory and not living animals.

Blood derived from stem cells could be used to help treat leukemia, sickle cell and other disorders.

Finally, the researchers injected these partially differentiated cells into sickle cell mice that had been treated with radiation to kill their own blood stem cells.

Blood from mice treated with iPS cells (above) does not show the sickle - shaped cells present in untreated mice (top).

Dr. Sharma theorized that the diagnosis of sleep disordered breathing could be missed in this population because adults with sickle cell disease are not generally obese, a common risk factor for apnea, and daytime sleepiness is attributed to the pain medications necessary to treat symptoms of the disease.

If X-SCID can be cured with no serious side effects, that will ease concerns about the risks of using similar vectors to treat other blood diseases such as sickle cell disease, notes Dunbar.

«Conversations with Innovators:» UNC hematologist on promising drug trials for treating painful crises in sickle cell patients

«Conversations with Innovators:» UNC hematologist on promising drug trials for treating painful crises in sickle cell patients -

«Conversations with Innovators:» UNC hematologist on promising drug trials for treating painful crises in sickle cell patients - Read More...

The study represents an important step toward more effectively treating certain patients with sickle cell disease who need frequent blood transfusions and currently have few options.

St. Jude has been committed to treating and curing sickle cell disease since its opening in 1962.

Kenneth Ataga, MD, director of the UNC Comprehensive Sickle Cell Program, was featured in a video by the American Society of Hematology in which he discussed the favorable results of a yearlong clinical trial studying crizanlizumab as a therapy to prevent and treat painful crisis events in patients with sickle cell diSickle Cell Program, was featured in a video by the American Society of Hematology in which he discussed the favorable results of a yearlong clinical trial studying crizanlizumab as a therapy to prevent and treat painful crisis events in patients with sickle cell diseCell Program, was featured in a video by the American Society of Hematology in which he discussed the favorable results of a yearlong clinical trial studying crizanlizumab as a therapy to prevent and treat painful crisis events in patients with sickle cell disickle cell disecell disease.

Endari, the first new treatment for patients with sickle cell disease in almost 20 years, Genentech's Hemlibra, the first - ever non-blood product to treat patients with hemophilia A with inhibitors, Actemra, the first treatment for adults diagnosed with giant cell arteritis, BioMarin's Brineura, the first treatment for a form of Batten disease, Benznidazole, the first U.S. treatment for Chagas disease, Novartis» Kymriah to treat certain children and young adults with B - cell acute lymphoblastic leukemia, which is also the first gene therapy to become available in the United States, are some of the drugs that received the FDA's stamp of approval in 2017.

Plasmapheresis can be used to treat a variety of disorders including: myasthenia gravis, Guillan - Barre syndrome, chronic inflammatory demyelinating polyneuropathy, Lamber - Eaton myasthenic syndrome, sickle cell disease, certain forms of neuropathies, Wilson's disease, and thrombotic thrombocytopenic purpura.

The company is also urging regulators to green - light a study on treating sickle - cell disease in people.

Gene editing has emerged as a promising strategy to treat diseases like β - thalassemia and sickle cell disease which are both caused by mutations in the gene for β - globin (HBB).

Along with treating children with malignant disease, he also will care for those whose blood disorders are not malignant, such as patients with sickle cell anemia.

Over eighty patients are treated on a chronic transfusion regimen, receiving their monthly transfusions either in the Sickle Cell Center outpatient clinic or at the pheresis center.

Generally, a hematologist treats patients with blood disorders, such as types of hemophilia, leukemia, lymphoma, and sickle cell anemia.

Been diagnosed with, been treated for or advised by a licensed member of the medical profession to receive treatment for Alzheimer's, dementia, memory loss, organic brain disease, mental incapacity, Lou Gehrig's disease (ALS), Down's Syndrome, Huntington's disease, sickle cell anemia, cystic fibrosis, cerebral palsy or been diagnosed by a medical professional as having a terminal medical condition that is expected to result in death within the next 18 months?