The study opens the door not only for
treating ALD, but also other neurological diseases.
An additional treatment modality used to
treat ALD is VNA.
Not exact matches
The terminally ill 23 - month - old, who was being
treated at
Alder Hey Children's Hospital in Liverpool, died at 2.30 am on Saturday, his parents Kate James and Thomas Evans said.
In February, Mr Justice Hayden ruled that doctors at
Alder Hey could stop
treating Alfie against the wishes of his parents following hearings in the Family Division of the High Court in London and Liverpool.
Some conditions on the screening list are relatively common, but
ALD is among the rare disorders the tests ferret out that can lead to serious health issues or even death if not detected and
treated, Botkin said.
• Combining stem cells with gene therapy, an international collaboration announced the success of a pilot study to
treat X-linked adrenoleukodystrophy (
ALD), a fatal brain disease caused by a mutation of the gene coding for the
ALD protein.
Doctors
treated 17 children with
ALD with gene therapy; two years later, 15 were functioning normally.
Since it was founded in 1914,
Alder Hey has led the way in the care of sick children,
treating more than 200,000 patients every year.