Sentences with phrase «treating inherited diseases»

That's a disadvantage when it comes to treating inherited diseases, but it means that diseases like cancer can be treated with less risk of side effects.

Tweaking these bugs — rather than the genes themselves — may be a way to treat inherited diseases and perhaps even protect against obesity.

The treatment, developed at the University of Pennsylvania with clinical trials carried out at Children's Hospital of Philadelphia and the University of Iowa, is the first time gene therapy is used to treat an inherited disease and could lead to treatments of other currently untreatable conditions.

Scientists at the University of North Carolina at Chapel Hill School of Medicine have devised a gene therapy cocktail that has the potential to treat some inherited diseases associated with «misfolded» proteins.

Not exact matches

The price is for Spark Therapeutics» Luxturna, approved by the Food and Drug Administration in December to treat a rare, inherited retinal disease that can lead to blindness.

And a third, different kind of gene therapy from Spark Therapeutics — to treat a rare inherited form of blindness — is likely to be approved by the end of 2017, too, making this year a landmark for treatments that manipulate the body's own biological mechanisms in novel new ways to fight deadly diseases.

«Gene - delivery system prevents vision loss from inherited eye disease: Initial testing in animal models holds promise for treating Leber congenital amauroisis and other congenital visual disorders.»

Their findings, showing the involvement of common immunity - related pathways, point toward potential new strategies for treating the late stages of inherited blinding diseases.

«Given that every newborn in the United States is screened for a number of inherited metabolic disorders, including MMA, there is a critical need for better understanding of the disease mechanisms and therapies to treat them.»

The transgenerational epigenetic mechanism of microRNA differed from a study that showed how treating the father's symptoms of an inherited disease can epigenetically treat the son.

Belgian researchers have identified a new strategy for treating an inherited form of dementia after attempting to turn stem cells derived from patients into the neurons most affected by the disease.

Gene therapy holds the promise to treat many inherited diseases.

Recent advances «give us reasonable hope that gene therapy will enter the armamentarium» to treat genetic blood disorders, some cancers, and inherited diseases, Fischer said, adding: «We might be very close to approval by regulatory authorities.»

This approach is also being used to treat eye diseases and hemophilia, an inherited disease that leads to a high risk for excess bleeding, even from minor cuts.

Transplanting fat may treat such inherited metabolic diseases as maple syrup urine disease (MSUD) by helping the body process the essential amino acids that these patients can not, according to Penn State College of Medicine researchers.

Meanwhile, researchers have treated another inherited childhood brain disease called Canavan disease with gene therapy.

For the first time, researchers have infused a person's blood with gene - editing tools, aiming to treat his severe inherited disease, The Associated Press (AP) reported today.

The findings open up an avenue for treating Huntington's as well as other inherited neurodegenerative diseases, although more testing of safety and long - term effects is needed, says senior author Xiao - Jiang Li, MD, PhD, distinguished professor of human genetics at Emory University School of Medicine.

National Institute of Dental and Craniofacial Research (NIDCR)-- Est. 1948 NIDCR provides leadership for a national research program designed to understand, treat, and ultimately prevent the infectious and inherited craniofacial - oral - dental diseases and disorders that compromise millions of human lives.

Mipomersen (Kynamro) reduces low - density lipoprotein (LDL) cholesterol by silencing a gene that produces apolipoprotein B - 100, a building block of LDL; the drug can treat familial hypercholesterolemia, an inherited disease that may cause heart attacks at an early age.

«Puppy lemon laws» which many states use to protect consumers sold dogs with infectious and / or inherited diseases and disorders do not apply to rescue / shelter dogs, so consumers are without recourse when treating their newly purchased dogs, often purchased sight unseen and with no medical history;

Constitutional homeopathy is the selection and administration of homeopathic preparations over a period of time to treat disorders caused by an inherited predisposition to a disease.

The dog has already played an important role in emerging therapies for inherited blindness in humans and similarities in disease phenotype and eye structure and function between dog and man, together with the increasingly sophisticated genetic tools that are available for the dog, mean that the dog is likely to play an ever increasing role in both our understanding of the normal functioning of the eye and in our ability to treat inherited eye disorders.

If your dog has any sort of disease or an inherited propensity for disease, ask your veterinarian about the benefits of nutritional therapy to help treat or prevent the disease.