Beta thalassemia is a genetic blood disorder where the body does not produce enough hemoglobin, which is needed for healthy red blood cells. This can lead to anemia and other health problems. Full definition
I've probably had over 10,000 needle sticks throughout my lifetime, because I have a genetic illness called Beta Thalassemia Major. (mindbodygreen.com)
Could Anti-Erythropoietin Receptor Antibodies Be the Future Management of Beta Thalassemia Intermedia? (thejh.org)
Biotech CRISPR Therapeutics is also joining the queue, as they use a similar approach in a clinical trial for beta thalassemia that's slated to begin this year in Europe. (frontlinegenomics.com)