After all, tests in many laboratories showed that providing normal copies of the gene should enable patients to make healthy copies of the protein specified by the gene. (scientificamerican.com)
It is injected into the eye and uses a benign virus to deliver healthy copies of the gene to the retina. (cnbc.com)
Doctors have been experimenting with gene therapy to supply healthy copies of a gene to patients suffering from a genetic defect. (newscientist.com)