A virus that has shown promise as a vector for human gene therapy causes liver tumors in neonatal mice. (science.sciencemag.org)
The first successful targeted human gene therapy was reported in 2000. (slu.edu)
Most recently, Dr. Gringeri was the Chief Operating Officer for Amsterdam Molecular Therapeutics (AMT), a Netherlands - based company engaged in human gene therapies for orphan diseases related to metabolic disorders, liver diseases, blood diseases, and disorders of the central and peripheral nervous systems. (viacyte.com)