The finding could lead to studies of a similar gene therapy to treat people with inherited blood disorders. (sciencedaily.com)
Sickle cell disease is a group of inherited blood disorders caused by genetic mutations in the HBB gene, resulting in abnormal hemoglobin, the iron - containing protein that normally allows blood cells to carry oxygen. (salk.edu)
Sickle cell anemia is the most common inherited blood disorder. (stjude.org)