We will recognize those individuals and organizations that have made extraordinary contributions to the Canadian rare disease community over this past year. (raredisorders.ca)
The Foundation believes that combinations could be highly beneficial to SMA patients and to the wider rare disease community. (smafoundation.org)
«Specifically, I think the exclusion of the OPEN Act is disappointing to the rare disease community,» she said, referring to the Orphan Product Extensions Now (OPEN) Act that was present in previous versions of the bill but left on the cutting room floor in its final form. (fortune.com)