«How the liver unclogs itself: Findings could potentially improve prognosis of infants with rare liver disease.» (sciencedaily.com)
Our first liver therapeutic development program is for methylmalonic acidemia (MMA), a serious and often life - threatening rare liver disease; it is primarily a pediatric disease with onset in early infancy. (modernatx.com)
Gelsinger had a rare liver disease and was participating in gene therapy research at the university when he died. (discovermagazine.com)