In this way, SOLVE - RD will have a significant impact on our knowledge and clinical practice when it comes to diagnosing and treating rare diseases in Europe. (cnag.cat)
But Moderna has had to retreat from optimistic predictions about a partnership with Alexion to treat a rare disease called Crigler - Najjar syndrome. (sciencemag.org)
The researchers will work directly with four European reference networks (or ERNs): European networks of care providers set up to share and enhance the knowledge and resources used for treating rare diseases. (www2.le.ac.uk)