Moreover, cells can dial gene expression up or down, adjusting to produce anywhere from a few working copies of a gene to several thousand. (sciencedaily.com)
The disorder occurs, Song says, when working copies of the gene for MeCP2 are silenced during development. (sciencedaily.com)
The technique replaces the defective gene response for cystic fibrosis by using inhaled molecules of DNA to deliver a normal working copy of the gene to lung cells. (sciencedaily.com)