Sentences with phrase «gene therapy drugs»

«Money back guarantee» for cell - gene therapy drug High prices for marketed cell / gene therapy products is a hot and controversial topic.

Human Stem Cell Institute (MICEX: ISKJ, Russia) HSCI just got an authorization for sales of the first gene therapy drug in Russia.

LONDON, April 12 - GlaxoSmithKline is divesting its rare disease gene therapy drugs to private biotech company Orchard Therapeutics as Chief Executive Emma Walmsley makes good on her promise to prune the drugmaker's pharmaceuticals portfolio.

In general, the requirements of FDA and EMA for authorization of gene therapy drugs have much in common with Russian requirements — safety and efficacy.

Allowing some of the economic benefit derived from the Orphan Drug Act to be used to lower the price of new gene therapy drugs.

Their product is a good candidate to become the first approved gene therapy drug in US.

a virus that can be used to deliver gene therapy drugs to cells.

LONDON, April 12 - GlaxoSmithKline is divesting its rare disease gene therapy drugs to Orchard Therapeutics, it said on Thursday, as Chief Executive Emma Walmsley makes good on her promise to prune the drugmaker's pharmaceuticals portfolio.

AAV is in use in many late - stage clinical trials in the United States, and has already been approved for use in one gene therapy drug in the European Union.

The new gene therapy drug will be available on Russian Federation pharmaceutical market in second quarter 2012 after the first batch certification process.

The first gene therapy drug was approved on the Russian market on December 7.

Michigan Technological University scientists have developed a process that could lead to stickier — and better — gene therapy drugs.

A single infusion of the gene therapy drug showed improved levels of the essential blood clotting protein Factor VIII, with 85 per cent of patients achieving normal or near - normal Factor VIII levels even many months after treatment.

Clinical researchers at Barts Health NHS Trust and Queen Mary University of London have found that over one year on from a single treatment with a gene therapy drug, participants with haemophilia A (the most common type) are showing normal levels of the previously missing protein, and effectively curing them.

This gene therapy drug from Xalud Therapeutics (XT - 150) has been tested in pet dogs that have chronic pain — osteoarthritis, dysplasia, neuropathic pain and disk degeneration — with remarkable results.

This led the team to package the gene editing tool into AAV, used in late - phase clinical trials in the U.S. and also already approved in a gene therapy drug in the European Union.

This week's headlines include: GSK slims portfolio with sale of rare disease gene therapy drugs, The Focus Shifts in Alzheimer's Research, Healing process after breast cancer surgery may trigger...

This week's headlines include: GSK slims portfolio with sale of rare disease gene therapy drugs, The...

GlaxoSmithKline Chief Executive, Emma Wamsley is keeping her promise to cut the drugmaker's pharmaceutical portfolio — the company said today that it is handing its rare disease gene therapy drugs to Orchard Therapeutics.

Unfortunately these requirements are not applicable for this sort of a gene therapy drug.

European regulators have recommended approval of the Western world's first gene therapy drug — after rejecting it on three previous...