Erlich, who is giving an update on the effort this week at the annual meeting of the American Society of Human Genetics in Vancouver, Canada, told ScienceInsider that although it's far short of even 1 million, he feels the project is on track and ready to move into new territory, such as working with disease advocacy groups. (sciencemag.org)
Dr. De Vivo emphasized that in developing drugs for orphan diseases such as SMA, collaborative programs are a must, and that «strong relationships with disease advocacy foundations are absolutely key.» (smafoundation.org)
The Blumberg Institute was established in 2003 as the research arm of the Hepatitis B Foundation, the nation's leading nonprofit research and disease advocacy organization solely dedicated to the global problem of hepatitis B. (blumberginstitute.org)